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Raising Rare - Raising Rare EPISODE 8, 6th June 2020
We Need Decisions that Lead to Therapies for GPX4

We Need Decisions that Lead to Therapies for GPX4

I am all-in for science. I actually get really excited when we discuss all the nerdy science details, but at the end of the day we want therapies and if this group cannot produce therapies, then we have failed in our responsibility. - Sanath Ramesh

We have previously shared the behind the scenes look at how Sanath and Ramya very rapidly adopted a virtual conference format due to the COVID outbreak.  

It turned out that this change served to enhance both the attendance and the effectiveness of the conference. It was a milestone in the search for a treatment and cure for baby Raghav. In this episode, we turn back to the conference to talk about the content and outcomes from that day.  

The importance and power of bringing experts in different fields together to focus on one problem just cannot be overstated.  

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