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Sifting Through Too Many Options
Episode 196th October 2021 • Raising Rare • Raising Rare
00:00:00 00:13:39

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We have been able to share some exciting news in the last two episodes. Sanath and cureGPX4.org commissioned a High-Throughput Screening assay to look for compounds that improve the growth of Raghav’s cells in culture. Then we heard the exciting news that the assay found 116 hits, 43 of which are already approved for other conditions.

Sanath has pulled together a team of experts to help him sift through this list of compounds and develop a plan for systematically assessing the various properties of these compounds. This is where the hard work begins. Approved medicines will have loads of data describing these properties. But there is much less data publicly available for investigational compounds.

Either way, the decision about what to try next is not going to be easy